Jada Bascom Foundation
All conditions

Inherited immune disorders

CD40 ligand deficiency

Also called: CD40LG deficiency · CD40L deficiency · HIGM1 · XHIGM · XHIM · CD154 deficiency · hyper IgM syndrome · primary immunodeficiency

What a donor has to do with this

For some people with this condition, a transplant using blood stem cells from an unrelated donor is part of the treatment guidelines. When a transplant is the right route and no one in the family matches, that donor comes from a registry. Not everyone with this condition has a transplant, and many never need one.

This is our reading of published transplant guidelines for this condition, not a measurement of how many people need a donor. Where a source actually counted donors, the figure and the people it counted are shown further down. Where none did, we say so rather than estimate.

What the evidence says

Who it affects
Typical onset/diagnosis: this X-linked disorder affects boys and men, usually presenting with infection in infancy or early childhood. Evidence: Europe/international EBMT/ESID guidance (2021); no markedly enriched geographic population was identified.
Treatments other than a transplant
Immunoglobulin replacement, antimicrobial prophylaxis, and infection-directed therapy — standard noncurative management — multiple regions — Long-term supportive care remains an alternative when HCT risk is unacceptable.
If a transplant is used, the cells come from
bone marrow: used in opened IEI transplant guidance; disease-specific share was not reported; mobilized peripheral blood stem cells: used in opened IEI transplant guidance; disease-specific share was not reported; umbilical cord blood: used as an alternative in opened IEI transplant guidance; disease-specific share was not reported; dominance: no dominant graft source was reported in the opened disease-specific sources
How often the donor was unrelated
Not reported. No source we could read states this for this condition, so we do not give a number. An estimate here would be a guess dressed as evidence.

Where this gets complicated

Published practice varies between early elective HCT and prolonged immunoglobulin-based management in clinically stable patients.; The disease should not be merged with autosomal-recessive CD40 deficiency or AID/UNG hyper-IgM syndromes, whose transplant indications differ.

People with this condition need donors

Joining a registry is a cheek swab and a short health form. You are contacted only if you turn out to be a possible match for someone, and you can ask questions and decline before anything else happens.

Related conditions

Others in inherited immune disorders. They are genuinely different diseases with different treatments — the group name is not a diagnosis.

Where this came from

CD40 ligand deficiency — what it is and how it is treated | Jada Bascom Foundation